Introduction: The National Health Insurance Bureau announced the adjustment results of national medical insurance drugs, and 74 new drugs entered the catalogue. A shot of 7, life-saving drugs has also entered medical insurance. What rare diseases can this medicine treat? 1. What rare diseases can this medicine treat? < P > Rare diseases are also called orphan diseases, which is a worldwide medical problem. The incidence of this disease is low, and it is generally rare. It is usually a genetic disease but it will endanger the life of patients. A 7,-shot life-saving drug is a prescription drug that can treat spinal muscular atrophy. According to the statistics of the Medical Insurance Bureau, there are about 1,2 new patients with spinal muscular atrophy, a rare disease of newborns in China. After this drug is included in medical insurance, it can reduce the economic burden for many patients. This medicine for treating rare diseases was close to 7, needles when it was first listed. Later, after an hour of negotiations, representatives of Chinese medicine enterprises gave everyone a satisfactory price. Second, what countries have done to treat rare diseases
At present, about 7, rare diseases have been found in the world, and 5% of them have effective therapeutic drugs, so patients all over the world are facing some drug shortages. In addition, the research and development cost of rare drugs is relatively high, and the high treatment cost has caused patients and their families to be financially unaffordable. With the efforts of the state, some new drugs for rare diseases will enter the medical insurance catalogue through negotiation every year. In addition to medical insurance, the state is still exploring more payment methods for these patients, such as commercial insurance and patient organization assistance, so as to increase the accessibility of patients to medicines. Each province has also established a special fund for the protection of rare diseases to provide protection for more patients with rare diseases. Third, what is spinal muscular atrophy < P > This disease is a chromosomal recessive genetic disease, mainly including infant type, delayed infant type and juvenile type. At the onset of the disease, it may cause muscle atrophy and weakness, and severe patients may die of respiratory paralysis, so the mortality rate of the disease is particularly high. Some patients will get sick within six months of birth. Patients with severe illness may have some obvious symptoms at birth, infants often have symptoms such as weakness of limbs and difficulty in feeding, and even some serious patients will die before they are two years old. Delayed babies may develop symptoms after six months of birth to one and a half years old.